
                                SEQUENCE LISTING

<110> Iversen, Patrick L.

<110> Sarepta Therapeutics, Inc.

<120> METHODS AND COMPOSITIONS FOR MANIPULATING TRANSLATION OF 
PROTEIN ISOFORMS FROM ALTERNATIVE INITIATION START SITES

<130> 120178.493PC

<140> PCT                  
<141> 2012-07-13

<150> 61/508,558
<151> 2011-07-15 

<160> 32

<170> FastSEQ for Windows Version 4.0

<210> 1
<211> 53
<212> RNA
<213> Homo sapiens

<400> 1
cugccuuccg ggucacugcc auggaggagc cgcagucaga uccuagcguc gag        53

<210> 2
<211> 53
<212> RNA
<213> Homo sapiens

<400> 2
cccccuugcc gucccaagca auggaugauu ugaugcuguc cccggacgau auu        53

<210> 3
<211> 22
<212> DNA
<213> Artificial Sequence

<220> 
<223> p53 targeting oligonucleotide

<400> 3
gcggctcctc catggcagtg ac                                          22

<210> 4
<211> 22
<212> DNA
<213> Artificial Sequence

<220> 
<223> p53 targeting oligonucleotide

<400> 4
catcaaatca tccattgctt gg                                          22

<210> 5
<211> 20
<212> DNA
<213> Artificial Sequence

<220> 
<223> p53 targeting oligonucleotide

<400> 5
agtttccata ggtctgaaaa                                             20

<210> 6
<211> 20
<212> DNA
<213> Artificial Sequence

<220> 
<223> p53 targeting oligonucleotide

<220> 
<221> modified_base  
<222> (2)...(4)
<223> I

<220> 
<221> modified_base  
<222> 15
<223> I

<400> 6
gnnnactgta gatgngtgaa                                             20

<210> 7
<211> 20
<212> DNA
<213> Artificial Sequence

<220> 
<223> p53 targeting oligonucleotide

<400> 7
cggataagat gctgaggagg                                             20

<210> 8
<211> 19
<212> DNA
<213> Artificial Sequence

<220> 
<223> p53 targeting oligonucleotide

<400> 8
gttgtagtgg atggtggta                                              19

<210> 9
<211> 20
<212> DNA
<213> Artificial Sequence

<220> 
<223> p53 targeting oligonucleotide

<400> 9
ctggagtctt ccagtgtgat                                             20

<210> 10
<211> 21
<212> DNA
<213> Artificial Sequence

<220> 
<223> p53 targeting oligonucleotide

<220> 
<221> modified_base  
<222> 4
<223> I

<400> 10
aagngtgaaa tattctccat c                                           21

<210> 11
<211> 19
<212> DNA
<213> Artificial Sequence

<220> 
<223> p53 targeting oligonucleotide

<400> 11
gcgctcacgc ccacggatc                                              19

<210> 12
<211> 20
<212> DNA
<213> Artificial Sequence

<220> 
<223> p53 targeting oligonucleotide

<400> 12
ccctgctccc ccctggctcc                                             20

<210> 13
<211> 22
<212> DNA
<213> Artificial Sequence

<220> 
<223> p53 targeting oligonucleotide

<400> 13
tgccatcaac atatcttgat cg                                          22

<210> 14
<211> 9
<212> PRT
<213> Artificial Sequence

<220> 
<223> Arginine-Rich Cell-Penetrating Peptide Transporter

<400> 14
Arg Arg Arg Gln Arg Arg Lys Lys Arg
 1               5                  


<210> 15
<211> 9
<212> PRT
<213> Artificial Sequence

<220> 
<223> Arginine-Rich Cell-Penetrating Peptide Transporter

<400> 15
Arg Lys Lys Arg Arg Gln Arg Arg Arg
 1               5                  


<210> 16
<211> 11
<212> PRT
<213> Artificial Sequence

<220> 
<223> Arginine-Rich Cell-Penetrating Peptide Transporter

<400> 16
Arg Arg Arg Arg Arg Arg Arg Arg Arg Phe Phe
 1               5                  10      


<210> 17
<211> 11
<212> PRT
<213> Artificial Sequence

<220> 
<223> Arginine-Rich Cell-Penetrating Peptide Transporter

<400> 17
Arg Arg Arg Arg Arg Phe Phe Arg Arg Arg Arg
 1               5                  10      


<210> 18
<211> 4
<212> PRT
<213> Artificial Sequence

<220> 
<223> Arginine-Rich Cell-Penetrating Peptide Transporter

<400> 18
Arg Arg Arg Arg
 1              


<210> 19
<211> 5
<212> PRT
<213> Artificial Sequence

<220> 
<223> Arginine-Rich Cell-Penetrating Peptide Transporter

<400> 19
Arg Arg Arg Arg Arg
 1               5  


<210> 20
<211> 6
<212> PRT
<213> Artificial Sequence

<220> 
<223> Arginine-Rich Cell-Penetrating Peptide Transporter

<400> 20
Arg Arg Arg Arg Arg Arg
 1               5      


<210> 21
<211> 7
<212> PRT
<213> Artificial Sequence

<220> 
<223> Arginine-Rich Cell-Penetrating Peptide Transporter

<400> 21
Arg Arg Arg Arg Arg Arg Arg
 1               5          


<210> 22
<211> 8
<212> PRT
<213> Artifcial Sequence

<220> 
<223> Arginine-Rich Cell-Penetrating Peptide Transporter

<400> 22
Arg Arg Arg Arg Arg Arg Arg Arg
 1               5              


<210> 23
<211> 9
<212> PRT
<213> Artificial Sequence

<220> 
<223> Arginine-Rich Cell-Penetrating Peptide Transporter

<400> 23
Arg Arg Arg Arg Arg Arg Arg Arg Arg
 1               5                  


<210> 24
<211> 16
<212> PRT
<213> Artificial Sequence

<220> 
<223> Arginine-Rich Cell-Penetrating Peptide Transporter

<220> 
<221> MOD_RES        
<222> 2, 4, 6, 8, 10, 12, 14, 16
<223> Acp

<400> 24
Arg Xaa Arg Xaa Arg Xaa Arg Xaa Arg Xaa Arg Xaa Arg Xaa Arg Xaa
 1               5                  10                  15      


<210> 25
<211> 12
<212> PRT
<213> Artificial Sequence

<220> 
<223> Arginine-Rich Cell-Penetrating Peptide Transporter

<220> 
<221> MOD_RES        
<222> 2, 5, 8, 11
<223> Acp

<400> 25
Arg Xaa Arg Arg Xaa Arg Arg Xaa Arg Arg Xaa Arg
 1               5                  10          


<210> 26
<211> 15
<212> PRT
<213> Artificial Sequence

<220> 
<223> Arginine-Rich Cell-Penetrating Peptide Transporter

<220> 
<221> MOD_RES        
<222> 2, 5, 8, 11, 14
<223> Acp

<400> 26
Arg Xaa Arg Arg Xaa Arg Arg Xaa Arg Arg Xaa Arg Arg Xaa Arg
 1               5                  10                  15  


<210> 27
<211> 12
<212> PRT
<213> Artificial Sequence

<220> 
<223> Arginine-Rich Cell-Penetrating Peptide Transporter

<220> 
<221> MOD_RES        
<222> 2, 8
<223> Acp

<220> 
<221> MOD_RES        
<222> 5, 11
<223> bAla

<400> 27
Arg Xaa Arg Arg Xaa Arg Arg Xaa Arg Arg Xaa Arg
 1               5                  10          


<210> 28
<211> 15
<212> PRT
<213> Artificial Sequence

<220> 
<223> Arginine-Rich Cell-Penetrating Peptide Transporter

<400> 28
Arg Ala Arg Arg Ala Arg Arg Ala Arg Arg Ala Arg Phe Phe Cys
 1               5                  10                  15  


<210> 29
<211> 15
<212> PRT
<213> Artificial Sequence

<220> 
<223> Arginine-Rich Cell-Penetrating Peptide Transporter

<400> 29
Arg Gly Arg Arg Gly Arg Arg Gly Arg Arg Gly Arg Phe Phe Cys
 1               5                  10                  15  


<210> 30
<211> 10
<212> RNA
<213> Homo Sapiens

<400> 1
tggctaaugc                                                             10


<210> 31
<211> 21
<212> RNA
<213> Homo Sapiens

<400> 2
aaggaaaaug gaugagacag a                                                21


<210> 32
<211> 22
<212> RNA
<213> Homo Sapiens

<400> 3
cgacugcaga cccaugacaa ga                                               22

