                         SEQUENCE LISTING

<110>  BESTWICK, Richard K.
       FRANK, Diane Elizabeth
 
<120>  IMPROVED EXON SKIPPING COMPOSITIONS FOR TREATING MUSCULAR 
       DYSTROPHY

<130>  AVN-010PC

<150>  US 61/739,968
<151>  2012-12-20

<160>  29    

<170>  PatentIn version 3.5

<210>  1
<211>  28
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic H53A(+33+60)

<400>  1
gttgcctccg gttctgaagg tgttcttg                                          28


<210>  2
<211>  25
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic H53A(+23+47)

<400>  2
ctgaaggtgt tcttgtactt catcc                                             25


<210>  3
<211>  30
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic H53A/2(+33+62)

<400>  3
ctgttgcctc cggttctgaa ggtgttcttg                                        30


<210>  4
<211>  33
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic H53A(+33+65)

<400>  4
caactgttgc ctccggttct gaaggtgttc ttg                                    33


<210>  5
<211>  25
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic h53A(+31+55)

<400>  5
ctccggttct gaaggtgttc ttgta                                             25


<210>  6
<211>  28
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic H53A(+46+73)

<400>  6
atttcattca actgttgcct ccggttct                                          28


<210>  7
<211>  25
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic H53A(+22+46)

<400>  7
tgaaggtgtt cttgtacttc atccc                                             25


<210>  8
<211>  24
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic H53A(+46+69)

<400>  8
cattcaactg ttgcctccgg ttct                                              24


<210>  9
<211>  22
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic H53A(+40+61)

<400>  9
tgttgcctcc ggttctgaag gt                                                22


<210>  10
<211>  9
<212>  PRT
<213>  Artificial Sequence

<220>
<223>  Synthetic rTAT

<400>  10

Arg Arg Arg Gln Arg Arg Lys Lys Arg 
1               5                   


<210>  11
<211>  9
<212>  PRT
<213>  Artificial Sequence

<220>
<223>  Synthetic Tat

<400>  11

Arg Lys Lys Arg Arg Gln Arg Arg Arg 
1               5                   


<210>  12
<211>  11
<212>  PRT
<213>  Artificial Sequence

<220>
<223>  Synthetic R9F2

<400>  12

Arg Arg Arg Arg Arg Arg Arg Arg Arg Phe Phe 
1               5                   10      


<210>  13
<211>  11
<212>  PRT
<213>  Artificial Sequence

<220>
<223>  Synthetic R5F2R4

<400>  13

Arg Arg Arg Arg Arg Phe Phe Arg Arg Arg Arg 
1               5                   10      


<210>  14
<211>  4
<212>  PRT
<213>  Artificial Sequence

<220>
<223>  Synthetic R4

<400>  14

Arg Arg Arg Arg 
1               


<210>  15
<211>  5
<212>  PRT
<213>  Artificial Sequence

<220>
<223>  Synthetic R5

<400>  15

Arg Arg Arg Arg Arg 
1               5   


<210>  16
<211>  6
<212>  PRT
<213>  Artificial Sequence

<220>
<223>  Synthetic R6

<400>  16

Arg Arg Arg Arg Arg Arg 
1               5       


<210>  17
<211>  7
<212>  PRT
<213>  Artificial Sequence

<220>
<223>  Synthetic R7

<400>  17

Arg Arg Arg Arg Arg Arg Arg 
1               5           


<210>  18
<211>  8
<212>  PRT
<213>  Artificial Sequence

<220>
<223>  Synthetic R8

<400>  18

Arg Arg Arg Arg Arg Arg Arg Arg 
1               5               


<210>  19
<211>  9
<212>  PRT
<213>  Artificial Sequence

<220>
<223>  Synthetic R9

<400>  19

Arg Arg Arg Arg Arg Arg Arg Arg Arg 
1               5                   


<210>  20
<211>  16
<212>  PRT
<213>  Artificial Sequence

<220>
<223>  Synthetic (RX)8


<220>
<221>  misc_feature
<222>  (2)..(2)
<223>  Xaa can be any naturally occurring amino acid

<220>
<221>  misc_feature
<222>  (4)..(4)
<223>  Xaa can be any naturally occurring amino acid

<220>
<221>  misc_feature
<222>  (6)..(6)
<223>  Xaa can be any naturally occurring amino acid

<220>
<221>  misc_feature
<222>  (8)..(8)
<223>  Xaa can be any naturally occurring amino acid

<220>
<221>  misc_feature
<222>  (10)..(10)
<223>  Xaa can be any naturally occurring amino acid

<220>
<221>  misc_feature
<222>  (12)..(12)
<223>  Xaa can be any naturally occurring amino acid

<220>
<221>  misc_feature
<222>  (14)..(14)
<223>  Xaa can be any naturally occurring amino acid

<220>
<221>  misc_feature
<222>  (16)..(16)
<223>  Xaa can be any naturally occurring amino acid

<400>  20

Arg Xaa Arg Xaa Arg Xaa Arg Xaa Arg Xaa Arg Xaa Arg Xaa Arg Xaa 
1               5                   10                  15      


<210>  21
<211>  12
<212>  PRT
<213>  Artificial Sequence

<220>
<223>  Synthetic (RAhxR)4; (P007)


<220>
<221>  misc_feature
<222>  (2)..(2)
<223>  Xaa is 6-aminohexanoic acid

<220>
<221>  misc_feature
<222>  (5)..(5)
<223>  Xaa is 6-aminohexanoic acid

<220>
<221>  misc_feature
<222>  (8)..(8)
<223>  Xaa is 6-aminohexanoic acid

<220>
<221>  misc_feature
<222>  (11)..(11)
<223>  Xaa is 6-aminohexanoic acid

<400>  21

Arg Xaa Arg Arg Xaa Arg Arg Xaa Arg Arg Xaa Arg 
1               5                   10          


<210>  22
<211>  15
<212>  PRT
<213>  Artificial Sequence

<220>
<223>  Synthetic (RAhxR)5; (CP04057)


<220>
<221>  misc_feature
<222>  (2)..(2)
<223>  Xaa is 6-aminohexanoic acid

<220>
<221>  misc_feature
<222>  (5)..(5)
<223>  Xaa is 6-aminohexanoic acid

<220>
<221>  misc_feature
<222>  (8)..(8)
<223>  Xaa is 6-aminohexanoic acid

<220>
<221>  misc_feature
<222>  (11)..(11)
<223>  Xaa is 6-aminohexanoic acid

<220>
<221>  misc_feature
<222>  (14)..(14)
<223>  Xaa is 6-aminohexanoic acid

<400>  22

Arg Xaa Arg Arg Xaa Arg Arg Xaa Arg Arg Xaa Arg Arg Xaa Arg 
1               5                   10                  15  


<210>  23
<211>  12
<212>  PRT
<213>  Artificial Sequence

<220>
<223>  Synthetic (RAhxRRBR)2;CP06062


<220>
<221>  misc_feature
<222>  (2)..(2)
<223>  Xaa is 6-aminohexanoic acid

<220>
<221>  misc_feature
<222>  (8)..(8)
<223>  Xaa is 6-aminohexanoic acid

<400>  23

Arg Xaa Arg Arg Asx Arg Arg Xaa Arg Arg Asx Arg 
1               5                   10          


<210>  24
<211>  14
<212>  PRT
<213>  Artificial Sequence

<220>
<223>  Synthetic (RAR)4F2

<400>  24

Arg Ala Arg Arg Ala Arg Arg Ala Arg Arg Ala Arg Phe Phe 
1               5                   10                  


<210>  25
<211>  14
<212>  PRT
<213>  Artificial Sequence

<220>
<223>  Synthetic (RGR)4F2

<400>  25

Arg Gly Arg Arg Gly Arg Arg Gly Arg Arg Gly Arg Phe Phe 
1               5                   10                  


<210>  26
<211>  23
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic Primer

<400>  26
cttggacaga acttaccgac tgg                                               23


<210>  27
<211>  23
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic Primer

<400>  27
gtttcttcca aagcagcctc tcg                                               23


<210>  28
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic Primer

<400>  28
gcaggatttg gaacagaggc g                                                 21


<210>  29
<211>  23
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic Primer

<400>  29
catctacatt tgtctgccac tgg                                               23


