                         SEQUENCE LISTING

<110>  University of Rochester
       Maquat, Lynne E.
       Kurosaki, Tatsuaki
 
<120>  COMPOSITIONS AND METHODS FOR TREATING DISEASES ASSOCIATED WITH 
       NONSENSE-MEDIATED DECAY RESISTANT mRNA

<130>  87550-949917 (129WO1)

<150>  US 62/037,424
<151>  2014-08-14

<160>  82    

<170>  PatentIn version 3.5

<210>  1
<211>  25
<212>  DNA
<213>  Artificial sequence

<220>
<223>  Synthetic construct

<400>  1
gtccaactca gccacatcaa aggtc                                             25


<210>  2
<211>  25
<212>  DNA
<213>  Artificial sequence

<220>
<223>  Synthetic construct

<400>  2
ccatatagga gaaggccgag tagag                                             25


<210>  3
<211>  15
<212>  DNA
<213>  Artificial sequence

<220>
<223>  Synthetic construct

<400>  3
actcagccac atcaa                                                        15


<210>  4
<211>  15
<212>  DNA
<213>  Artificial sequence

<220>
<223>  Synthetic construct

<400>  4
agaaggccga gtaga                                                        15


<210>  5
<211>  24
<212>  DNA
<213>  Artificial sequence

<220>
<223>  Synthetic construct

<400>  5
ctaaccgcta tttcttatct tgcg                                              24


<210>  6
<211>  15
<212>  DNA
<213>  Artificial sequence

<220>
<223>  Synthetic construct

<400>  6
tttcttatcc ttgcg                                                        15


<210>  7
<211>  19
<212>  RNA
<213>  Artificial sequence

<220>
<223>  Synthetic construct

<400>  7
gaugcaguuc cgcuccauu                                                    19


<210>  8
<211>  20
<212>  RNA
<213>  Artificial sequence

<220>
<223>  Synthetic construct

<400>  8
cuagugagau aauuagucca                                                   20


<210>  9
<211>  19
<212>  RNA
<213>  Artificial sequence

<220>
<223>  Synthetic construct

<400>  9
ggagaagcga guaacccug                                                    19


<210>  10
<211>  19
<212>  RNA
<213>  Artificial sequence

<220>
<223>  Synthetic construct

<400>  10
ccaggacacg aggaaacug                                                    19


<210>  11
<211>  19
<212>  RNA
<213>  Artificial sequence

<220>
<223>  Synthetic construct

<400>  11
caaguacuau aauguggaa                                                    19


<210>  12
<211>  19
<212>  RNA
<213>  Artificial sequence

<220>
<223>  Synthetic construct

<400>  12
ggcugauuuc uguaacaua                                                    19


<210>  13
<211>  19
<212>  RNA
<213>  Artificial sequence

<220>
<223>  Synthetic construct

<400>  13
gcuugaucuc uauaggcaa                                                    19


<210>  14
<211>  19
<212>  RNA
<213>  Artificial sequence

<220>
<223>  Synthetic construct

<400>  14
gucaaccauu ggaggacaa                                                    19


<210>  15
<211>  19
<212>  RNA
<213>  Artificial sequence

<220>
<223>  Synthetic construct

<400>  15
aguggaauuc gagaccagc                                                    19


<210>  16
<211>  19
<212>  RNA
<213>  Artificial sequence

<220>
<223>  Synthetic construct

<400>  16
agaugaacuu accguagaa                                                    19


<210>  17
<211>  19
<212>  RNA
<213>  Artificial sequence

<220>
<223>  Synthetic construct

<400>  17
uaaccaagcu gcaaucaug                                                    19


<210>  18
<211>  19
<212>  RNA
<213>  Artificial sequence

<220>
<223>  Synthetic construct

<400>  18
gagguucgau guccaguua                                                    19


<210>  19
<211>  25
<212>  RNA
<213>  Artificial sequence

<220>
<223>  Synthetic construct

<400>  19
ucaagagccu cugcgagaag gcuaa                                             25


<210>  20
<211>  31
<212>  DNA
<213>  Artificial sequence

<220>
<223>  Synthetic construct

<400>  20
acgcctgcag ttactctgga atacacgatc c                                      31


<210>  21
<211>  25
<212>  DNA
<213>  Artificial sequence

<220>
<223>  Synthetic construct

<400>  21
aatcgacgaa agcacccagg ccacc                                             25


<210>  22
<211>  24
<212>  DNA
<213>  Artificial sequence

<220>
<223>  Synthetic construct

<400>  22
gatagcggcc gcttaatact gggc                                              24


<210>  23
<211>  30
<212>  DNA
<213>  Artificial sequence

<220>
<223>  Synthetic construct

<400>  23
ggaattctgg cgggcgcggg cgctgcggcg                                        30


<210>  24
<211>  20
<212>  DNA
<213>  Artificial sequence

<220>
<223>  Synthetic construct

<400>  24
aaggcccggt accgcttctc                                                   20


<210>  25
<211>  31
<212>  DNA
<213>  Artificial sequence

<220>
<223>  Synthetic construct

<400>  25
ggtgacgagt ttaaagcaca aatcgacgtg g                                      31


<210>  26
<211>  27
<212>  DNA
<213>  Artificial sequence

<220>
<223>  Synthetic construct

<400>  26
gtgacggggc tggcccagta ttaaaag                                           27


<210>  27
<211>  76
<212>  DNA
<213>  Artificial sequence

<220>
<223>  Synthetic construct

<400>  27
gtggatcctg agaacttcag gctcctgggc aacgtgctgg tctgtgtgct ggcccatcac       60

tttggcaaag aattca                                                       76


<210>  28
<211>  26
<212>  DNA
<213>  Artificial sequence

<220>
<223>  Synthetic construct

<400>  28
atatctcgag atgagccaag gccccc                                            26


<210>  29
<211>  36
<212>  DNA
<213>  Artificial sequence

<220>
<223>  Synthetic construct

<400>  29
gcgctcgagt tatcaaccaa tttccttcca ctgctt                                 36


<210>  30
<211>  31
<212>  DNA
<213>  Artificial sequence

<220>
<223>  Synthetic construct

<400>  30
cgatcgcata tgcggtacga ggacgcctac c                                      31


<210>  31
<211>  65
<212>  DNA
<213>  Artificial sequence

<220>
<223>  Synthetic construct

<400>  31
caatgcctcg aggctgcctc ctcctgtctc tggtaatcct ccgctgaact gcatgaggct       60

ctcac                                                                   65


<210>  32
<211>  12
<212>  DNA
<213>  Artificial sequence

<220>
<223>  Synthetic construct

<400>  32
aagggtagac ca                                                           12


<210>  33
<211>  14
<212>  DNA
<213>  Artificial sequence

<220>
<223>  Synthetic construct

<400>  33
ttgaggttgt ccag                                                         14


<210>  34
<211>  13
<212>  DNA
<213>  Artificial sequence

<220>
<223>  Synthetic construct

<400>  34
tgccaaagtg atg                                                          13


<210>  35
<211>  21
<212>  DNA
<213>  Artificial sequence

<220>
<223>  Synthetic construct

<400>  35
accaccgtag aacgcagatc g                                                 21


<210>  36
<211>  21
<212>  DNA
<213>  Artificial sequence

<220>
<223>  Synthetic construct

<400>  36
cacgatcata ttgcccagga g                                                 21


<210>  37
<211>  21
<212>  DNA
<213>  Artificial sequence

<220>
<223>  Synthetic construct

<400>  37
accaccgtag aacgcagatc g                                                 21


<210>  38
<211>  24
<212>  DNA
<213>  Artificial sequence

<220>
<223>  Synthetic construct

<400>  38
cttctcacca ttcacctcgc actt                                              24


<210>  39
<211>  16
<212>  DNA
<213>  Artificial sequence

<220>
<223>  Synthetic construct

<400>  39
ctgatggggc tctatg                                                       16


<210>  40
<211>  18
<212>  DNA
<213>  Artificial sequence

<220>
<223>  Synthetic construct

<400>  40
tcctggtgag aagtctcc                                                     18


<210>  41
<211>  20
<212>  DNA
<213>  Artificial sequence

<220>
<223>  Synthetic construct

<400>  41
tctgccgtta ctgccctgtg                                                   20


<210>  42
<211>  21
<212>  DNA
<213>  Artificial sequence

<220>
<223>  Synthetic construct

<400>  42
cacgatcata ttgcccagga g                                                 21


<210>  43
<211>  24
<212>  DNA
<213>  Artificial sequence

<220>
<223>  Synthetic construct

<400>  43
cggtttcccg tgcaatcagt tcgg                                              24


<210>  44
<211>  24
<212>  DNA
<213>  Artificial sequence

<220>
<223>  Synthetic construct

<400>  44
tcaccattca cctcgcactt ctca                                              24


<210>  45
<211>  19
<212>  DNA
<213>  Artificial sequence

<220>
<223>  Synthetic construct

<400>  45
acggaaccct caaacagac                                                    19


<210>  46
<211>  24
<212>  DNA
<213>  Artificial sequence

<220>
<223>  Synthetic construct

<400>  46
gtagttggac ttagggaaca aagg                                              24


<210>  47
<211>  20
<212>  DNA
<213>  Artificial sequence

<220>
<223>  Synthetic construct

<400>  47
actgtgttca ctagcaaccc                                                   20


<210>  48
<211>  20
<212>  DNA
<213>  Artificial sequence

<220>
<223>  Synthetic construct

<400>  48
caggagtcag atgcaccatg                                                   20


<210>  49
<211>  18
<212>  DNA
<213>  Artificial sequence

<220>
<223>  Synthetic construct

<400>  49
ccaaaggaga ccatctga                                                     18


<210>  50
<211>  24
<212>  DNA
<213>  Artificial sequence

<220>
<223>  Synthetic construct

<400>  50
gtagttggac ttagggaaca aagg                                              24


<210>  51
<211>  18
<212>  DNA
<213>  Artificial sequence

<220>
<223>  Synthetic construct

<400>  51
ccaaaggaga ccatctga                                                     18


<210>  52
<211>  17
<212>  DNA
<213>  Artificial sequence

<220>
<223>  Synthetic construct

<400>  52
cctcatctcg gctttcc                                                      17


<210>  53
<211>  36
<212>  DNA
<213>  Artificial sequence

<220>
<223>  Synthetic construct


<220>
<221>  misc_feature
<223>  n is inosine

<400>  53
ggccacgcgt cgactagtac gggnngggnn gggnng                                 36


<210>  54
<211>  20
<212>  DNA
<213>  Artificial sequence

<220>
<223>  Synthetic construct

<400>  54
ggccacgcgt cgactagtac                                                   20


<210>  55
<211>  24
<212>  DNA
<213>  Artificial sequence

<220>
<223>  Synthetic construct

<400>  55
gtagttggac ttagggaaca aagg                                              24


<210>  56
<211>  18
<212>  DNA
<213>  Artificial sequence

<220>
<223>  Synthetic construct

<400>  56
ccaaaggaga ccatctga                                                     18


<210>  57
<211>  17
<212>  DNA
<213>  Artificial sequence

<220>
<223>  Synthetic construct

<400>  57
cctcatctcg gctttcc                                                      17


<210>  58
<211>  20
<212>  DNA
<213>  Artificial sequence

<220>
<223>  Synthetic construct

<400>  58
ggaggaattc tcggctggag                                                   20


<210>  59
<211>  19
<212>  DNA
<213>  Artificial sequence

<220>
<223>  Synthetic construct

<400>  59
cgttatcggg gtcgacgtt                                                    19


<210>  60
<211>  20
<212>  DNA
<213>  Artificial sequence

<220>
<223>  Synthetic construct

<400>  60
ttgcagggaa cccaactacc                                                   20


<210>  61
<211>  23
<212>  DNA
<213>  Artificial sequence

<220>
<223>  Synthetic construct

<400>  61
tccttccatt gagatgaatg tgg                                               23


<210>  62
<211>  20
<212>  DNA
<213>  Artificial sequence

<220>
<223>  Synthetic construct

<400>  62
ttgtctcctg gtcacgaacc                                                   20


<210>  63
<211>  20
<212>  DNA
<213>  Artificial sequence

<220>
<223>  Synthetic construct

<400>  63
tgtggcagca actcaacaga                                                   20


<210>  64
<211>  21
<212>  DNA
<213>  Artificial sequence

<220>
<223>  Synthetic construct

<400>  64
gatgaatgtg tgagtcagac c                                                 21


<210>  65
<211>  21
<212>  DNA
<213>  Artificial sequence

<220>
<223>  Synthetic construct

<400>  65
gcagacgata catcaggata c                                                 21


<210>  66
<211>  19
<212>  DNA
<213>  Artificial sequence

<220>
<223>  Synthetic construct

<400>  66
aatcgtgcgt gacattaag                                                    19


<210>  67
<211>  20
<212>  DNA
<213>  Artificial sequence

<220>
<223>  Synthetic construct

<400>  67
atgatggagt tgaaggtagt                                                   20


<210>  68
<211>  20
<212>  DNA
<213>  Artificial sequence

<220>
<223>  Synthetic construct

<400>  68
gtcgccagcc gagccacatc                                                   20


<210>  69
<211>  20
<212>  DNA
<213>  Artificial sequence

<220>
<223>  Synthetic construct

<400>  69
ccaggcgccc aatacgacca                                                   20


<210>  70
<211>  19
<212>  DNA
<213>  Artificial sequence

<220>
<223>  Synthetic construct

<400>  70
cacagggcag taacggcag                                                    19


<210>  71
<211>  21
<212>  DNA
<213>  Artificial sequence

<220>
<223>  Synthetic construct

<400>  71
gaatccagat gctcaaggcc c                                                 21


<210>  72
<211>  17
<212>  DNA
<213>  Artificial sequence

<220>
<223>  Synthetic construct

<400>  72
cctcatctcg gctttcc                                                      17


<210>  73
<211>  21
<212>  DNA
<213>  Artificial sequence

<220>
<223>  Synthetic construct

<400>  73
gaatccagat gctcaaggcc c                                                 21


<210>  74
<211>  17
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic construct

<400>  74
cctcatctcg gctttcc                                                      17


<210>  75
<211>  17
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic construct

<400>  75
cctcatctcg gctttcc                                                      17


<210>  76
<211>  50
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  Synthetic construct

<400>  76
caaaacaaaa caaaacaaca auagcuacug cagacucucu cucucucguc                  50


<210>  77
<211>  76
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  Synthetic construct

<400>  77
gggagugaaa cgauguucua cguaaaagaa cgccaacaac aacaacaaca acaagguuuu       60

ucuucugaag auaaag                                                       76


<210>  78
<211>  96
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic construct

<400>  78
ctttatcttc agaagaaaaa ccttgttgtt gttgttgttg ttggcgttct tttacgtaga       60

acatcgtttc actccctata gtgagtcgta ttagaa                                 96


<210>  79
<211>  15
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic construct

<400>  79
cattagccac accag                                                        15


<210>  80
<211>  15
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic construct

<400>  80
gtgatacttg tgggc                                                        15


<210>  81
<211>  25
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic construct

<400>  81
gtggtggccc agcacaatca cgatc                                             25


<210>  82
<211>  25
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic construct

<400>  82
ggccactcca gccaccacct tctgg                                             25


