                         SEQUENCE LISTING

<110>  THE CHARLOTTE MECKLENBURG HOSPITAL AUTHORITY D/B/A 
       CAROLINAS HEALTHCARE SYSTEM
       Long Lu, Qi
 
<120>  METHODS AND COMPOSITIONS FOR TREATING DYSTROGLYCANOPATHY 
       DISORDERS

<130>  1184-9

<150>  US 62/126,271
<151>  2015-02-27

<160>  2     

<170>  PatentIn version 3.5

<210>  1
<211>  1488
<212>  DNA
<213>  Artificial

<220>
<223>  Optimized nucleotide coding sequence for FKRP

<400>  1
atgagactga caagatgcca ggccgccctg gccgctgcca tcacactgaa tctgctggtg       60

ctgttctatg tgtcctggct gcagcaccag ccccggaact ctagagccag aggcccaaga      120

agggcctctg ccgccggacc tagagtgaca gtgctcgtgc gcgagttcga ggccttcgac      180

aatgccgtgc ccgagctggt ggacagcttc ctgcagcaag accctgctca gcctgtggtg      240

gtggccgccg atacactgcc ttatcctcca ctggccctgc ccagaatccc caatgtgcga      300

ctggctctgc tgcagcccgc cctggataga cctgccgccg ctagcagacc tgagacatac      360

gtggccaccg agttcgtggc cctggtgcct gatggcgcca gagctgaagc tcccggcctg      420

ctggaaagaa tggtggaagc cctgagagcc ggcagcgcca gactggtggc tgctcctgtg      480

gctaccgcca accctgccag atgtctggcc ctgaatgtgt ccctgagaga gtggaccgcc      540

agatacggcg ctgcccctgc cgctcctaga tgtgatgctc tggatggcga cgccgtggtg      600

ctgctgagag ccagggacct gttcaacctg agcgcccctc tggccagacc tgtgggcaca      660

agcctgtttc tgcagacagc cctgaggggc tgggccgtgc agctgctgga tctgacattt      720

gccgctgcca gacagcctcc tctggccaca gcccatgcca gatggaaggc cgagagagag      780

ggcagagcca gaagggctgc tctgctgagg gccctgggca tcagactggt gtcttgggaa      840

ggcggcagac tcgagtggtt cggctgcaac aaagaaacca cccggtgctt cggcaccgtc      900

gtgggcgata caccagccta cctgtacgag gaaagatgga cccccccttg ctgcctgcgg      960

gccctgagag aaacagccag atatgtcgtg ggcgtgctgg aagccgctgg cgtgcgatat     1020

tggctggaag gcggatctct gctgggagcc gccaggcacg gcgacatcat cccttgggac     1080

tacgacgtgg acctgggcat ctacctggaa gatgtgggca actgcgagca gctgagaggc     1140

gccgaagccg gctctgtggt ggatgagagg ggcttcgtgt gggagaaggc cgtggaaggc     1200

gacttcttcc gggtgcagta cagcgagagc aaccatctgc atgtggacct gtggcccttc     1260

tacccccgga acggcgtgat gaccaaggac acctggctgg accaccggca ggacgtggaa     1320

ttccccgagc actttctgca gcccctggtg ccactgcctt tcgccggatt tgtggcccag     1380

gcccccaaca actaccggcg gttcctggaa ctgaagttcg gccctggcgt gatcgagaac     1440

ccccagtacc ctaaccctgc cctgctgagc ctgaccggca gcggctaa                  1488


<210>  2
<211>  1488
<212>  DNA
<213>  Homo sapiens

<400>  2
atgcggctca cccgctgcca ggctgccctg gcggccgcca tcaccctcaa ccttctggtc       60

ctcttctatg tctcgtggct gcagcaccag cctaggaatt cccgggcccg ggggccccgt      120

cgtgcctctg ctgccggccc ccgtgtcacc gtcctggtgc gggagttcga ggcatttgac      180

aacgcggtgc ccgagctggt agactccttc ctgcagcaag acccagccca gcccgtggtg      240

gtggcagccg acacgctccc ctacccgccc ctggccctgc cccgcatccc caacgtgcgt      300

ctggcgctgc tccagcccgc cctggaccgg ccagccgcag cctcgcgccc ggagacctac      360

gtggccaccg agtttgtggc cctagtacct gatggggcgc gggctgaggc acctggcctg      420

ctggagcgca tggtggaggc gctccgcgca ggaagcgcac gtctggtggc cgccccggtt      480

gccacggcca accctgccag gtgcctggcc ctgaacgtca gcctgcgaga gtggaccgcc      540

cgctatggcg cagcccccgc cgcgccccgc tgcgacgccc tggacggaga tgctgtggtg      600

ctcctgcgcg cccgcgacct cttcaacctc tcggcgcccc tggcccggcc ggtgggcacc      660

agcctctttc tgcagaccgc ccttcgcggc tgggcggtgc agctgctgga cttgaccttc      720

gccgcggcgc gccagccccc gctggccacg gcccacgcgc gctggaaggc tgagcgcgag      780

ggacgcgctc ggcgggcggc gctgctccgc gcgctgggca tccgcctagt gagctgggaa      840

ggcgggcggc tggagtggtt cggctgcaac aaggagacca cgcgctgctt cggaaccgtg      900

gtgggcgaca cgcccgccta cctctacgag gagcgctgga cgcccccctg ctgcctgcgc      960

gcgctgcgcg agaccgcccg ctatgtggtg ggcgtgctgg aggctgcggg cgtgcgctac     1020

tggctcgagg gcggctcact gctgggggcc gcccgccacg gggacatcat cccatgggac     1080

tacgacgtgg acctgggcat ctacttggag gacgtgggca actgcgagca gctgcggggg     1140

gcagaggccg gctcggtggt ggatgagcgc ggcttcgtat gggagaaggc ggtcgagggc     1200

gactttttcc gcgtgcagta cagcgaaagc aaccacttgc acgtggacct gtggcccttc     1260

tacccccgca atggcgtcat gaccaaggac acgtggctgg accaccggca ggatgtggag     1320

tttcccgagc acttcctgca gccgctggtg cccctgccct ttgccggctt cgtggcgcag     1380

gcgcctaaca actaccgccg cttcctggag ctcaagttcg ggcccggggt catcgagaac     1440

ccccagtacc ccaacccggc actgctgagt ctgacgggaa gcggctga                  1488


