                         SEQUENCE LISTING

<110>  Mourich, Dan
 
<120>  ANTISENSE-INDUCED EXON EXCLUSION IN TYPE VII COLLAGEN

<130>  67463.00216

<140>  Not yet assigned
<151>  2016-06-01

<150>  62/169,454
<151>  2015-06-01

<160>  26    

<170>  PatentIn version 3.5

<210>  1
<211>  63
<212>  DNA
<213>  Homo sapiens

<400>  1
ggtctgcagg gtccaagagg cccccctggc ccagtggtga gtacccaaga accttcacct       60

gtc                                                                     63


<210>  2
<211>  22
<212>  DNA
<213>  Artificial sequence

<220>
<223>  Antisense oligomer


<220>
<221>  misc_feature
<222>  (1)..(2)
<223>  N is uracil (U) or thymine (T)

<220>
<221>  misc_feature
<222>  (6)..(6)
<223>  N is uracil (U) or thymine (T)

<220>
<221>  misc_feature
<222>  (9)..(9)
<223>  N is uracil (U) or thymine (T)

<220>
<221>  misc_feature
<222>  (16)..(16)
<223>  N is uracil (U) or thymine (T)

<400>  2
nngggnacnc accacngggc ca                                                22


<210>  3
<211>  22
<212>  DNA
<213>  Artificial sequence

<220>
<223>  Antisense oligomer


<220>
<221>  misc_feature
<222>  (2)..(3)
<223>  N is uracil (U) or thymine (T)

<220>
<221>  misc_feature
<222>  (5)..(6)
<223>  N is uracil (U) or thymine (T)

<220>
<221>  misc_feature
<222>  (10)..(10)
<223>  N is uracil (U) or thymine (T)

<220>
<221>  misc_feature
<222>  (13)..(13)
<223>  N is uracil (U) or thymine (T)

<220>
<221>  misc_feature
<222>  (20)..(20)
<223>  N is uracil (U) or thymine (T)

<400>  3
gnncnngggn acncaccacn gg                                                22


<210>  4
<211>  22
<212>  DNA
<213>  Artificial sequence

<220>
<223>  Antisense oligomer


<220>
<221>  misc_feature
<222>  (5)..(6)
<223>  N is uracil (U) or thymine (T)

<220>
<221>  misc_feature
<222>  (8)..(9)
<223>  N is uracil (U) or thymine (T)

<220>
<221>  misc_feature
<222>  (13)..(13)
<223>  N is uracil (U) or thymine (T)

<220>
<221>  misc_feature
<222>  (16)..(16)
<223>  N is uracil (U) or thymine (T)

<400>  4
aaggnncnng ggnacncacc ac                                                22


<210>  5
<211>  22
<212>  DNA
<213>  Artificial sequence

<220>
<223>  Antisense oligomer


<220>
<221>  misc_feature
<222>  (6)..(6)
<223>  N is uracil (U) or thymine (T)

<220>
<221>  misc_feature
<222>  (12)..(13)
<223>  N is uracil (U) or thymine (T)

<220>
<221>  misc_feature
<222>  (15)..(16)
<223>  N is uracil (U) or thymine (T)

<220>
<221>  misc_feature
<222>  (20)..(20)
<223>  N is uracil (U) or thymine (T)

<400>  5
acaggngaag gnncnngggn ac                                                22


<210>  6
<211>  22
<212>  DNA
<213>  Artificial sequence

<220>
<223>  Antisense oligomer


<220>
<221>  misc_feature
<222>  (3)..(3)
<223>  N is uracil (U) or thymine (T)

<220>
<221>  misc_feature
<222>  (6)..(6)
<223>  N is uracil (U) or thymine (T)

<220>
<221>  misc_feature
<222>  (13)..(13)
<223>  N is uracil (U) or thymine (T)

<220>
<221>  misc_feature
<222>  (21)..(21)
<223>  N is inosine (I)

<400>  6
ggnacncacc acngggccag ng                                                22


<210>  7
<211>  22
<212>  DNA
<213>  Artificial sequence

<220>
<223>  Antisense oligomer


<220>
<221>  misc_feature
<222>  (6)..(6)
<223>  N is uracil (U) or thymine (T)

<220>
<221>  misc_feature
<222>  (8)..(8)
<223>  N is inosine (I)

<220>
<221>  misc_feature
<222>  (14)..(14)
<223>  N is inosine (I)

<220>
<221>  misc_feature
<222>  (16)..(16)
<223>  N is inosine (I)

<220>
<221>  misc_feature
<222>  (18)..(18)
<223>  N is inosine (I)

<220>
<221>  misc_feature
<222>  (21)..(21)
<223>  N is uracil (U) or thymine (T)

<400>  7
accacngngc cagngngncc nc                                                22


<210>  8
<211>  24
<212>  DNA
<213>  Artificial sequence

<220>
<223>  Antisense oligomer


<220>
<221>  misc_feature
<222>  (5)..(5)
<223>  N is uracil (U) or thymine (T)

<220>
<221>  misc_feature
<222>  (7)..(8)
<223>  N is uracil (U) or thymine (T)

<220>
<221>  misc_feature
<222>  (15)..(15)
<223>  N is uracil (U) or thymine (T)

<220>
<221>  misc_feature
<222>  (24)..(24)
<223>  N is uracil (U) or thymine (T)

<400>  8
ggccncnngg acccngcaga cccn                                              24


<210>  9
<211>  9
<212>  PRT
<213>  Artificial sequence

<220>
<223>  Synthetic peptide

<400>  9

Arg Arg Arg Gln Arg Arg Lys Lys Arg 
1               5                   


<210>  10
<211>  9
<212>  PRT
<213>  Artificial sequence

<220>
<223>  Synthetic peptide

<400>  10

Arg Lys Lys Arg Arg Gln Arg Arg Arg 
1               5                   


<210>  11
<211>  11
<212>  PRT
<213>  Artificial sequence

<220>
<223>  Synthetic peptide

<400>  11

Arg Arg Arg Arg Arg Arg Arg Arg Arg Phe Phe 
1               5                   10      


<210>  12
<211>  11
<212>  PRT
<213>  Artificial sequence

<220>
<223>  Synthetic peptide

<400>  12

Arg Arg Arg Arg Arg Phe Phe Arg Arg Arg Arg 
1               5                   10      


<210>  13
<211>  4
<212>  PRT
<213>  Artificial sequence

<220>
<223>  Synthetic peptide

<400>  13

Arg Arg Arg Arg 
1               


<210>  14
<211>  5
<212>  PRT
<213>  Artificial sequence

<220>
<223>  Synthetic peptide

<400>  14

Arg Arg Arg Arg Arg 
1               5   


<210>  15
<211>  6
<212>  PRT
<213>  Artificial sequence

<220>
<223>  Synthetic peptide

<400>  15

Arg Arg Arg Arg Arg Arg 
1               5       


<210>  16
<211>  7
<212>  PRT
<213>  Artificial sequence

<220>
<223>  Synthetic peptide

<400>  16

Arg Arg Arg Arg Arg Arg Arg 
1               5           


<210>  17
<211>  8
<212>  PRT
<213>  Artificial sequence

<220>
<223>  Synthetic peptide

<400>  17

Arg Arg Arg Arg Arg Arg Arg Arg 
1               5               


<210>  18
<211>  9
<212>  PRT
<213>  Artificial sequence

<220>
<223>  Synthetic peptide

<400>  18

Arg Arg Arg Arg Arg Arg Arg Arg Arg 
1               5                   


<210>  19
<211>  16
<212>  PRT
<213>  Artificial sequence

<220>
<223>  Synthetic peptide


<220>
<221>  misc_feature
<222>  (2)..(2)
<223>  Xaa can be any naturally occurring amino acid

<220>
<221>  misc_feature
<222>  (4)..(4)
<223>  Xaa can be any naturally occurring amino acid

<220>
<221>  misc_feature
<222>  (6)..(6)
<223>  Xaa can be any naturally occurring amino acid

<220>
<221>  misc_feature
<222>  (8)..(8)
<223>  Xaa can be any naturally occurring amino acid

<220>
<221>  misc_feature
<222>  (10)..(10)
<223>  Xaa can be any naturally occurring amino acid

<220>
<221>  misc_feature
<222>  (12)..(12)
<223>  Xaa can be any naturally occurring amino acid

<220>
<221>  misc_feature
<222>  (14)..(14)
<223>  Xaa can be any naturally occurring amino acid

<220>
<221>  misc_feature
<222>  (16)..(16)
<223>  Xaa can be any naturally occurring amino acid

<400>  19

Arg Xaa Arg Xaa Arg Xaa Arg Xaa Arg Xaa Arg Xaa Arg Xaa Arg Xaa 
1               5                   10                  15      


<210>  20
<211>  12
<212>  PRT
<213>  Artificial sequence

<220>
<223>  Synthetic peptide


<220>
<221>  MISC_FEATURE
<222>  (2)..(2)
<223>  X is 6-aminohexanoic acid

<220>
<221>  MISC_FEATURE
<222>  (5)..(5)
<223>  X is 6-aminohexanoic acid

<220>
<221>  MISC_FEATURE
<222>  (8)..(8)
<223>  X is 6-aminohexanoic acid

<220>
<221>  MISC_FEATURE
<222>  (11)..(11)
<223>  X is 6-aminohexanoic acid

<400>  20

Arg Xaa Arg Arg Xaa Arg Arg Xaa Arg Arg Xaa Arg 
1               5                   10          


<210>  21
<211>  15
<212>  PRT
<213>  Artificial sequence

<220>
<223>  Synthetic peptide


<220>
<221>  MISC_FEATURE
<222>  (2)..(2)
<223>  X is 6-aminohexanoic acid

<220>
<221>  MISC_FEATURE
<222>  (5)..(5)
<223>  X is 6-aminohexanoic acid

<220>
<221>  MISC_FEATURE
<222>  (8)..(8)
<223>  X is 6-aminohexanoic acid

<220>
<221>  MISC_FEATURE
<222>  (11)..(11)
<223>  X is 6-aminohexanoic acid

<220>
<221>  MISC_FEATURE
<222>  (14)..(14)
<223>  X is 6-aminohexanoic acid

<400>  21

Arg Xaa Arg Arg Xaa Arg Arg Xaa Arg Arg Xaa Arg Arg Xaa Arg 
1               5                   10                  15  


<210>  22
<211>  12
<212>  PRT
<213>  Artificial sequence

<220>
<223>  Synthetic peptide


<220>
<221>  MISC_FEATURE
<222>  (2)..(2)
<223>  X is 6-aminohexanoic acid

<220>
<221>  MISC_FEATURE
<222>  (5)..(5)
<223>  X is beta-alanine

<220>
<221>  MISC_FEATURE
<222>  (8)..(8)
<223>  X is 6-aminohexanoic acid

<220>
<221>  MISC_FEATURE
<222>  (11)..(11)
<223>  X is beta-alanine

<400>  22

Arg Xaa Arg Arg Xaa Arg Arg Xaa Arg Arg Xaa Arg 
1               5                   10          


<210>  23
<211>  14
<212>  PRT
<213>  Artificial sequence

<220>
<223>  Synthetic peptide

<400>  23

Arg Ala Arg Arg Ala Arg Arg Ala Arg Arg Ala Arg Phe Phe 
1               5                   10                  


<210>  24
<211>  14
<212>  PRT
<213>  Artificial sequence

<220>
<223>  Synthetic peptide

<400>  24

Arg Gly Arg Arg Gly Arg Arg Gly Arg Arg Gly Arg Phe Phe 
1               5                   10                  


<210>  25
<211>  19
<212>  DNA
<213>  Artificial sequence

<220>
<223>  Forward primer

<400>  25

taccaggaga gcgtggtat                                                    19


<210>  26
<211>  18
<212>  DNA
<213>  Artificial sequence

<220>
<223>  Reverse primer

<400>  26

gtcctggagg tcctgtct                                                     18
