                         SEQUENCE LISTING

<110>  INSERM (Institut National de la Sant et de la Recherche 
       Mdicale)
       Universit d'Evry-Val-d'Essonne
       GENETHON
       Fondazione Istituto Italiano di Tecnologia
 
<120>  A VECTOR AND PHARMACEUTICAL COMPOSITION FOR REDUCING THE 
       EXPRESSION OF NKCC1 IN A SUBJECT IN NEED THEREOF, AS WELL AS THE 
       RELATED THERAPEUTIC TREATMENT METHOD

<130>  PC1585EC-BRE-EC

<150>  EP17305434
<151>  2017-04-11

<160>  92    

<170>  PatentIn version 3.5

<210>  1
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  amiR sequence

<400>  1
ttccacactt actaccacat c                                                 21


<210>  2
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  amiR sequence

<400>  2
tacatatcca catccctcat a                                                 21


<210>  3
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  amiR sequence

<400>  3
tatacatatc cacatccctc a                                                 21


<210>  4
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  amiR sequence

<400>  4
tccacactta ctaccacatc c                                                 21


<210>  5
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  amiR sequence

<400>  5
tattccacac ttactaccac a                                                 21


<210>  6
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  amiR sequence

<400>  6
ttaacctgat ctgccggtat g                                                 21


<210>  7
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  amiR sequence

<400>  7
taagcaactc caccacggtt t                                                 21


<210>  8
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  amiR sequence

<400>  8
atatccacat ccctcatatc t                                                 21


<210>  9
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  amiR sequence

<400>  9
atacatatcc acatccctca t                                                 21


<210>  10
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  amiR sequence

<400>  10
attccacact tactaccaca t                                                 21


<210>  11
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  amiR sequence

<400>  11
atattccaca cttactacca c                                                 21


<210>  12
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  amiR sequence

<400>  12
taacctgatc tgccggtatg t                                                 21


<210>  13
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  amiR sequence

<400>  13
atttaacctg atctgccggt a                                                 21


<210>  14
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  amiR sequence

<400>  14
tgaatagaag gtaaggacac t                                                 21


<210>  15
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  amiR sequence

<400>  15
atgaatagaa ggtaaggaca c                                                 21


<210>  16
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  amiR sequence

<400>  16
tacaaggact gatagaccta t                                                 21


<210>  17
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  amiR sequence

<400>  17
ttacaaggac tgatagacct a                                                 21


<210>  18
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  amiR sequence

<400>  18
attacaagga ctgatagacc t                                                 21


<210>  19
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  amiR sequence

<400>  19
ttaagcaact ccaccacggt t                                                 21


<210>  20
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  amiR sequence

<400>  20
acgaattgaa tgctgcagtg c                                                 21


<210>  21
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  amiR sequence

<400>  21
ctcattatct gttattcgcc a                                                 21


<210>  22
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  amiR sequence

<400>  22
aatagaaggt aaggacactc t                                                 21


<210>  23
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  amiR sequence

<400>  23
tactaataca cccttgatcc a                                                 21


<210>  24
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  amiR sequence

<400>  24
tattgctgaa gtagacaatc c                                                 21


<210>  25
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  amiR sequence

<400>  25
aatccaacca catacatagc a                                                 21


<210>  26
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  amiR sequence

<400>  26
ttccttaagc aactccacca c                                                 21


<210>  27
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  amiR sequence

<400>  27
aattgaatgc tgcagtgcat t                                                 21


<210>  28
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  amiR sequence

<400>  28
atccacatcc ctcatatctg c                                                 21


<210>  29
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  amiR sequence

<400>  29
tatccacatc cctcatatct g                                                 21


<210>  30
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  amiR sequence

<400>  30
cacacttact accacatcct t                                                 21


<210>  31
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  amiR sequence

<400>  31
ttcaacagtg gttgagttgc a                                                 21


<210>  32
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  amiR sequence

<400>  32
agcaaagtag ccatcgctct c                                                 21


<210>  33
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  amiR sequence

<400>  33
aagcaaagta gccatcgctc t                                                 21


<210>  34
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  amiR sequence

<400>  34
taagcaaagt agccatcgct c                                                 21


<210>  35
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  amiR sequence

<400>  35
acttgctaag caaagtagcc a                                                 21


<210>  36
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  amiR sequence

<400>  36
aacttgctaa gcaaagtagc c                                                 21


<210>  37
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  amiR sequence

<400>  37
aacctgatct gccggtatgt c                                                 21


<210>  38
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  amiR sequence

<400>  38
ttctgcagta tacgtgacca c                                                 21


<210>  39
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  amiR sequence

<400>  39
acaacgtact aatacaccct t                                                 21


<210>  40
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  amiR sequence

<400>  40
catacaacgt actaatacac c                                                 21


<210>  41
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  amiR sequence

<400>  41
tgttccttaa gcaactccac c                                                 21


<210>  42
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  amiR sequence

<400>  42
aggagtgttc ctttgggtat g                                                 21


<210>  43
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  amiR sequence

<400>  43
taggagtgtt cctttgggta t                                                 21


<210>  44
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  amiR sequence

<400>  44
ctaggagtgt tcctttgggt a                                                 21


<210>  45
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  amiR sequence

<400>  45
agaacctaca gatactgcaa t                                                 21


<210>  46
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  amiR sequence

<400>  46
tcattaacgt ttccagtggc a                                                 21


<210>  47
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  amiR sequence

<400>  47
tgtcattaac gtttccagtg g                                                 21


<210>  48
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  amiR sequence

<400>  48
aatcctgaca ccatactcat t                                                 21


<210>  49
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  amiR sequence

<400>  49
aaatcctgac accatactca t                                                 21


<210>  50
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  amiR sequence

<400>  50
tcactaggga tgctaatgct g                                                 21


<210>  51
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  amiR sequence

<400>  51
tacagcccaa ggactatcac a                                                 21


<210>  52
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  amiR sequence

<400>  52
tatacagccc aaggactatc a                                                 21


<210>  53
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  amiR sequence

<400>  53
aagacgaatt gaatgctgca g                                                 21


<210>  54
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  amiR sequence

<400>  54
aagacgaatt gaatgctgca g                                                 21


<210>  55
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  amiR sequence

<400>  55
tttcatggct tgtcttcgag g                                                 21


<210>  56
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  amiR sequence

<400>  56
atctgcttgc aaccaatctt t                                                 21


<210>  57
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  amiR sequence

<400>  57
atatctgctt gcaaccaatc t                                                 21


<210>  58
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  amiR sequence

<400>  58
catatctgct tgcaaccaat c                                                 21


<210>  59
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  amiR sequence

<400>  59
aacagtggtt gagttgcagt c                                                 21


<210>  60
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  amiR sequence

<400>  60
ttgctaagca aagtagccat c                                                 21


<210>  61
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  amiR sequence

<400>  61
attatctgtt attcgccatg g                                                 21


<210>  62
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  amiR sequence

<400>  62
agctcattat ctgttattcg c                                                 21


<210>  63
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  amiR sequence

<400>  63
tgggtatcat aatagtagtg c                                                 21


<210>  64
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  amiR sequence

<400>  64
gtgggtatca taatagtagt g                                                 21


<210>  65
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  amiR sequence

<400>  65
acctattcca gcttgaccca c                                                 21


<210>  66
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  amiR sequence

<400>  66
caaaggcgaa gattagacca a                                                 21


<210>  67
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  amiR sequence

<400>  67
aaagaatcac gactgtaatg g                                                 21


<210>  68
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  amiR sequence

<400>  68
aacacaagaa cctacagata c                                                 21


<210>  69
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  amiR sequence

<400>  69
agtacagttt gttagctctg t                                                 21


<210>  70
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  amiR sequence

<400>  70
ttaatttgca ggctgcagaa g                                                 21


<210>  71
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  amiR sequence

<400>  71
ttgggagcac tcactaggga t                                                 21


<210>  72
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  amiR sequence

<400>  72
tttgggagca ctcactaggg a                                                 21


<210>  73
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  amiR sequence

<400>  73
aatgcatatg atgcaaggaa g                                                 21


<210>  74
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  amiR sequence

<400>  74
ctgcagtgca ttcaggtaag t                                                 21


<210>  75
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  amiR sequence

<400>  75
tgctgcagtg cattcaggta a                                                 21


<210>  76
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  amiR sequence

<400>  76
ttgaatgctg cagtgcattc a                                                 21


<210>  77
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  amiR sequence

<400>  77
tctctttcat ggcttgtctt c                                                 21


<210>  78
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  amiR sequence

<400>  78
ttggcttgat cgatggacat c                                                 21


<210>  79
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  amiR sequence

<400>  79
ttgagttgca gtcttgccat c                                                 21


<210>  80
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  amiR sequence

<400>  80
tttcaacagt ggttgagttg c                                                 21


<210>  81
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  amiR sequence

<400>  81
gaacttgcta agcaaagtag c                                                 21


<210>  82
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  amiR sequence

<400>  82
aagtctatcc ggaacttgct a                                                 21


<210>  83
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  amiR sequence

<400>  83
aactcattta acctgatctg c                                                 21


<210>  84
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  amiR sequence

<400>  84
taaccatgcc atgtagagag c                                                 21


<210>  85
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  amiR sequence

<400>  85
ttctaaccat gccatgtaga g                                                 21


<210>  86
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  amiR sequence

<400>  86
ctttgggtat ggctgactga g                                                 21


<210>  87
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  amiR sequence

<400>  87
ttcctttggg tatggctgac t                                                 21


<210>  88
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  amiR sequence

<400>  88
atacatagca actgcaacag c                                                 21


<210>  89
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  amiR sequence

<400>  89
agatgttgtc cttacataga g                                                 21


<210>  90
<211>  26
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  5'flanking region

<400>  90
tggaggcttg ctgaaggctg tatgct                                            26


<210>  91
<211>  19
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  loop forming sequence

<400>  91
gttttggcca ctgactgac                                                    19


<210>  92
<211>  46
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  3' flanking region

<400>  92
caggacacaa ggcctgttac tagcactcac atggaacaaa tggccc                      46


