                         SEQUENCE LISTING

<110>  ELOXX PHARMACEUTICALS, INC.
 
<120>  METHODS, COMPOSITIONS, AND KITS FOR INDUCING READTHROUGH

<130>  128570-8010.WO00

<140>  PCT/US 19/36171
<141>  2019-06-07

<150>  US 62/682,134
<151>  2018-06-07

<150>  US 62/773,090
<151>  2018-11-29

<150>  US 62/792,845
<151>  2019-01-15

<150>  US 62/857,787
<151>  2019-06-05

<160>  21    

<170>  PatentIn version 3.5

<210>  1
<211>  22
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  CFTR-1 forward primer

<400>  1
cattgcagtg ggctgtaaac tc                                                22


<210>  2
<211>  25
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  CFTR-1 reverse primer

<400>  2
cttctgttgg catgtcaatg aactt                                             25


<210>  3
<211>  18
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  hGAPDH forward primer

<400>  3
gcatcttctt ttgcgtcg                                                     18


<210>  4
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  MH hGAPDH reverse primer

<400>  4
tgtaaaccat gtagttgagg t                                                 21


<210>  5
<211>  15
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  CFTR2 S466X


<220>
<221>  misc_feature
<222>  (7)..(9)
<223>  Nucleotides of nonsense mutation

<400>  5
aagacuugac uucua                                                        15


<210>  6
<211>  15
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  CFTR2 G542X


<220>
<221>  misc_feature
<222>  (7)..(9)
<223>  Nucleotides of nonsense mutation

<400>  6
guucuuugag aaggu                                                        15


<210>  7
<211>  15
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  CFTR2 R1162X


<220>
<221>  misc_feature
<222>  (7)..(9)
<223>  Nucleotides of nonsense mutation

<400>  7
gugagcugag ucuuu                                                        15


<210>  8
<211>  15
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  CFTR2 C225X


<220>
<221>  misc_feature
<222>  (7)..(9)
<223>  Nucleotides of nonsense mutation

<400>  8
gccuucugag gacuu                                                        15


<210>  9
<211>  15
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  CFTR2 R553X


<220>
<221>  misc_feature
<222>  (7)..(9)
<223>  Nucleotides of nonsense mutation

<400>  9
ggucaaugag caaga                                                        15


<210>  10
<211>  15
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  CFTR2 S1455X


<220>
<221>  misc_feature
<222>  (7)..(9)
<223>  Nucleotides of nonsense mutation

<400>  10
cggaacugaa gcaag                                                        15


<210>  11
<211>  15
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  CFTR2 W1282X


<220>
<221>  misc_feature
<222>  (7)..(9)
<223>  Nucleotides of nonsense mutation

<400>  11
caacagugaa ggaaa                                                        15


<210>  12
<211>  15
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  CFTR2 R1158X


<220>
<221>  misc_feature
<222>  (7)..(9)
<223>  Nucleotides of nonsense mutation

<400>  12
uugaugugau cugug                                                        15


<210>  13
<211>  15
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  CFTR2 Y1092X (C-G)


<220>
<221>  misc_feature
<222>  (7)..(9)
<223>  Nucleotides of nonsense mutation

<400>  13
uucuuguagc uguca                                                        15


<210>  14
<211>  15
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  CFTR2 W1089X


<220>
<221>  misc_feature
<222>  (7)..(9)
<223>  Nucleotides of nonsense mutation

<400>  14
gccaacuagu ucuug                                                        15


<210>  15
<211>  15
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  CFTR2 Q552X


<220>
<221>  misc_feature
<222>  (7)..(9)
<223>  Nucleotides of nonsense mutation

<400>  15
ggagguuaac gagca                                                        15


<210>  16
<211>  15
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  CFTR2 Y1092X (C-A)


<220>
<221>  misc_feature
<222>  (7)..(9)
<223>  Nucleotides of nonsense mutation

<400>  16
uucuuguaac uguca                                                        15


<210>  17
<211>  15
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  CFTR2 Q890X


<220>
<221>  misc_feature
<222>  (7)..(9)
<223>  Nucleotides of nonsense mutation

<400>  17
ccucuuuaag acaaa                                                        15


<210>  18
<211>  15
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  CFTR2 K710X


<220>
<221>  misc_feature
<222>  (7)..(9)
<223>  Nucleotides of nonsense mutation

<400>  18
auacgauaau uuucc                                                        15


<210>  19
<211>  15
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  CFTR2 S1255X


<220>
<221>  misc_feature
<222>  (7)..(9)
<223>  Nucleotides of nonsense mutation

<400>  19
uuguuauaag cuuuu                                                        15


<210>  20
<211>  15
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  CFTR2 E585X


<220>
<221>  misc_feature
<222>  (7)..(9)
<223>  Nucleotides of nonsense mutation

<400>  20
gaaaaauaaa uauuu                                                        15


<210>  21
<211>  15
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  CFTR2 E92X


<220>
<221>  misc_feature
<222>  (7)..(9)
<223>  Nucleotides of nonsense mutation

<400>  21
uuaggguaag ucacc                                                        15


