               SEQUENCE LISTING

<110> GENETHON

<120> NEW GENE THERAPY FOR THE TREATMENT OF DUCHENNE MUSCULAR DYSTROPHY 

<130> G143-B-61574 PCT

<150> US63122703
<151> 2020-12-08

<160> 1

<170> BiSSAP 1.3.6

<210> 1
<211> 4640
<212> DNA
<213> Artificial Sequence


<220> 
<223> AAV_ITR_Spc512-human MD1

<400> 1
gcgcgctcgc tcgctcactg aggccgcccg ggcaaagccc gggcgtcggg cgacctttgg       60

tcgcccggcc tcagtgagcg agcgagcgcg cagagaggga gtggccaact ccatcactag      120

gggttccttg tagttaatga ttaacccgcc atgctactta tctacgtagc catgctctag      180

acatggctcg acagatcgag ctccaccgcg gtggcggccg tccgccctcg gcaccatcct      240

cacgacaccc aaatatggcg acgggtgagg aatggtgggg agttattttt agagcggtga      300

ggaaggtggg caggcagcag gtgttggcgc tctaaaaata actcccggga gttattttta      360

gagcggagga atggtggaca cccaaatatg gcgacggttc ctcacccgtc gccatatttg      420

ggtgtccgcc ctcggccggg gccgcattcc tgggggccgg gcggtgctcc cgcccgcctc      480

gataaaaggc tccggggccg gcggcggccc acgagctacc cggaggagcg ggaggcgcca      540

agctctagaa ctagtggatc ccccgggctg caggaattcg ccaccatgct gtggtgggag      600

gaagtggagg actgctacga gagagaggac gtgcagaaga aaaccttcac caagtgggtg      660

aacgcccagt tcagcaagtt cggcaagcag cacatcgaga acctgttcag cgacctgcag      720

gatggcagga gactgctgga tctgctggag ggactgaccg gccagaagct gcccaaggag      780

aagggcagca ccagagtgca cgccctgaac aacgtgaaca aggccctgag agtgctgcag      840

aacaacaacg tggacctggt gaatatcggc agcaccgaca tcgtggacgg caaccacaag      900

ctgaccctgg gcctgatctg gaacatcatc ctgcactggc aggtgaagaa cgtgatgaag      960

aacatcatgg ccggcctgca gcagaccaac agcgagaaga tcctgctgag ctgggtgagg     1020

cagagcacca gaaactaccc ccaggtgaac gtgatcaact tcaccacctc ctggagcgac     1080

ggcctggccc tgaacgccct gatccacagc cacagacccg acctgttcga ctggaacagc     1140

gtggtgtgtc agcagagcgc cacccagaga ctggagcacg ccttcaacat cgccagatac     1200

cagctgggca tcgagaagct gctggacccc gaggacgtgg acaccaccta ccccgacaag     1260

aaaagcatcc tgatgtatat tacctctctg tttcaggtgc tgccccagca ggtgtccatc     1320

gaggccatcc aggaagtgga aatgctgccc aggcccccca aagtgaccaa ggaggagcac     1380

ttccagctgc accaccagat gcactatagc cagcagatca ccgtgtccct ggcccagggc     1440

tatgagagaa ccagcagccc caagcccaga ttcaagagct acgcctacac ccaggccgcc     1500

tacgtgacca cctccgaccc caccagaagc cccttcccca gccagcacct ggaggccccc     1560

gaggacaaga gcttcggcag cagcctgatg gagagcgaag tgaacctgga cagataccag     1620

accgccctgg aggaagtgct gtcttggctg ctgtccgccg aggacaccct gcaggcccag     1680

ggcgagatca gcaacgacgt ggaagtggtg aaggaccagt tccacaccca cgagggctac     1740

atgatggatc tgaccgccca ccagggcaga gtgggcaata tcctgcagct gggcagcaag     1800

ctgatcggca ccggcaagct gagcgaggac gaggagaccg aagtgcagga gcagatgaac     1860

ctgctgaaca gcagatggga gtgcctgaga gtggccagca tggagaagca gagcaacctg     1920

caccgcgtgc tgatggacct gcagaaccag aagctgaagg agctgaacga ctggctgacc     1980

aagaccgagg agcggaccag aaagatggag gaggagcccc tgggccccga cctggaggac     2040

ctgaagagac aggtgcagca gcacaaagtg ctgcaggagg acctggaaca ggagcaggtg     2100

cgcgtgaaca gcctgaccca catggtggtc gtggtggacg agagcagcgg cgaccacgcc     2160

acagccgccc tggaagagca gctgaaagtg ctgggcgaca gatgggccaa catctgccgg     2220

tggaccgagg acagatgggt gctgctgcag gacatcctgc tgaagtggca gagactgaca     2280

gaggagcagt gcctgtttag cgcctggctg agcgagaagg aggacgccgt gaacaagatc     2340

cacaccaccg gcttcaagga ccagaacgag atgctgagca gcctgcagaa gctggccgtg     2400

ctgaaggccg atctggagaa gaaaaagcag agcatgggca agctgtactc cctgaagcag     2460

gacctgctgt ccaccctgaa gaacaagagc gtgacccaga aaaccgaggc ctggctggac     2520

aatttcgccc ggtgctggga caatctggtg cagaaactgg agaagagcac cgcccagatc     2580

agccaggccg tgaccaccac ccagcccagc ctgacacaga ccaccgtgat ggagaccgtg     2640

accacagtga ccaccaggga gcagatcctg gtgaagcacg cccaggagga gctgccccct     2700

cccccccctc agaagaagcg gcagatcaca gtggacaccc tggagagact gcaggagctg     2760

caggaagcca ccgacgagct ggacctgaag ctgagacagg ccgaagtgat caagggcagc     2820

tggcagcctg tgggcgatct gctgatcgac agcctgcagg accacctgga gaaagtgaag     2880

gccctgcggg gcgagatcgc ccccctgaag gagaatgtga gccacgtgaa cgacctggcc     2940

agacagctga ccaccctggg catccagctg agcccctaca atctgagcac cctggaagat     3000

ctgaacaccc ggtggaaact gctgcaggtg gccgtggagg atagagtgag gcagctgcac     3060

gaggcccaca gagacttcgg ccctgcctcc cagcacttcc tgagcaccag cgtgcagggc     3120

ccctgggaga gagccatctc ccccaacaaa gtgccctact acatcaacca cgagacccag     3180

accacctgct gggaccaccc taagatgacc gagctgtacc agagcctggc cgacctgaac     3240

aatgtgcggt tcagcgccta cagaaccgcc atgaagctgc ggagactgca gaaggccctg     3300

tgcctggacc tgctgagcct gagcgccgcc tgcgacgccc tggaccagca caacctgaag     3360

cagaacgacc agcccatgga cattctgcag atcatcaact gcctgaccac catctacgat     3420

cggctggagc aggagcacaa caacctggtg aacgtgcccc tgtgcgtgga catgtgcctg     3480

aattggctgc tgaacgtgta cgacaccggc aggaccggca gaatcagagt gctgtccttc     3540

aagaccggca tcatcagcct gtgcaaggcc cacctggagg ataagtaccg ctacctgttc     3600

aagcaggtgg ccagcagcac cggcttctgc gatcagagga gactgggcct gctgctgcac     3660

gatagcatcc agatccctag gcagctgggc gaagtggcca gctttggcgg cagcaacatc     3720

gagccctctg tgaggagctg cttccagttc gccaacaaca agcccgagat cgaggccgcc     3780

ctgttcctgg attggatgag gctggagccc cagagcatgg tgtggctgcc tgtgctgcac     3840

agagtggccg ccgccgagac cgccaagcac caggccaagt gcaacatctg caaggagtgc     3900

cccatcatcg gcttccggta caggagcctg aagcacttca actacgacat ctgccagagc     3960

tgctttttca gcggcagagt ggccaagggc cacaagatgc actaccccat ggtggagtac     4020

tgcaccccca ccacctccgg cgaggatgtg agagacttcg ccaaagtgct gaagaataag     4080

ttccggacca agcggtactt tgccaagcac cccaggatgg gctacctgcc cgtgcagacc     4140

gtgctggagg gcgacaacat ggagaccgac accatgtgat gatgagcggc cgcttccctt     4200

tagtgagggt taatgcttcg agcagacatg ataagataca ttgatgagtt tggacaaacc     4260

acaactagaa tgcagtgaaa aaaatgcttt atttgtgaaa tttgtgatgc tattgcttta     4320

tttgtaacca ttataagctg caataaacaa gttaacaaca acaattgcat tcattttatg     4380

tttcaggttc agggggagat gtgggaggtt ttttaaagca agtaaaacct ctacaaatgt     4440

ggtaaaatcc gataaggact agagcatggc tacgtagata agtagcatgg cgggttaatc     4500

attaactaca aggaacccct agtgatggag ttggccactc cctctctgcg cgctcgctcg     4560

ctcactgagg ccgggcgacc aaaggtcgcc cgacgcccgg gctttgcccg ggcggcctca     4620

gtgagcgagc gagcgcgcag                                                 4640


